Miplyffa (Arimoclomol Citrate): Uses, Side Effects & Interactions
1. Introduction and Mechanism of Action for Miplyffa Miplyffa is an orally administered, targeted cellular therapy containing the active pharmaceutical ingredient arimoclomol citrate, exclusively indicated for the management of neurological manifestations in patients with Niemann-Pick disease type C. The most notable side effects include severe gastrointestinal distress, significant unintended weight loss, and potential renal impairment. … Read more